Knowledge is Power: Part 2

The concluding episode of the Knowledge is Power series. The knowledge we are gaining at n-Lorem has even more value than benefiting nano-rare patients and their families. These insights will enable scientists to discover new therapeutic targets for both common and rare diseases, fundamentally changing the way we approach health and disease.


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On This Episode We Discuss:

• Questions we can answer and teach us about health and disease and opportunities to treat more common diseases


• What are all the functions of human genes?


• Are there gene products that have redundant functions?


• Do identical mutations cause identical phenotypes?


• n-Lorem can demonstrate that ASOs work on general types of disease challenges