March Forward

What if we told you that AI is helping us find new uses for existing medicines, bringing us closer to treatments for rare diseases? 🔍 🔬 💡

In this episode of March Forward, we gently explore how Artifi…

Have you ever felt that living with a rare or chronic illness comes with an unseen weight, a battle fought not just in the body, but in the mind too? 🧠

In this episode of March Forward, we gently expl…

The search for a rare disease diagnosis can be a long and lonely journey. But what if advanced technology could help light the way? 

In this episode of March Forward, we’re exploring SHEPHERD, an inno…

Is inflammation the hidden key in your rare disease journey? 🤔

For millions living with these complex conditions, understanding the body's fiery response is absolutely crucial to managing progression …

Imagine your body's best defenders—your immune cells—are ready for duty but locked away, unable to fight. 🛡️ For individuals with the ultra-rare WHIM syndrome, this isn't just an idea; it's the biolo…

What if the the cutting-edge science behind Beqvez, including its AAV vector and the high-activity FIX-Padua variant, relentless cycle of infusions for Hemophilia B could finally pause, allowing your…

What happens when standard treatments for a rare cancer like synovial sarcoma fall short? Could the answer lie in empowering your own immune system? 🛡️

In this episode of March Forward, we explore Afa…

What if we could gently fix the tiny genetic 'typos' that cause devastating rare diseases, right where they are in the body? 🧬

In this episode of March Forward, we dive into In Vivo CRISPR Base Editin…