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Major FDA approvals for Vertex/CRISPR; bluebird gets black box warning and price scrutiny

Author
BioSpace
Published
Wed 13 Dec 2023
Episode Link
https://podcasters.spotify.com/pod/show/biospace/episodes/Major-FDA-approvals-for-VertexCRISPR-bluebird-gets-black-box-warning-and-price-scrutiny-e2d6278

That was Week with a capital W. Two major FDA approvals for sickle cell came through on Friday - Casgevy, the first-ever CRISPR-based gene editing therapy from Vertex and CRISPR Therapeutics, and bluebird bio’s Lyfgenia, which comes with a hefty price tag and a black box warning. 


Axcella announced its closure; what does the future of long-covid treatments look like, especially as attention shifts to different markets like ADCs and neurological treatments? 


Also discussed - Vanda drops $100m on rights to MS drug Ponvory, AI regulatory developments in Europe. 


BioSpace's Lori Ellis, Greg Slabodkin and Tyler Patchen discuss.

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